Potency of Orphan Drugs

Orphan drugs are considered to be medicinal products future for the diagnosis, prevention or the treatment of rare diseases. Authorisation of all drugs in rare diseases disorders must be based on effectiveness of substantial evidence of effectiveness in preventing the condition with the evidence of safety for the treatment use. Over the last decade of 30 years, more than 400 medicines representing 447 separate medicinal indications have been approved to treat disorders and diseases symptoms rare diseases, compared to lesser than 10 in the 1970s.